index - Organisation de la cellule musculaire et thérapie de la myopathie centronucléaire autosomique dominante

Dernières publications

Chiffres clés

Chargement de la page

Open Access

55 %

Mots clés

Cancer Duchenne muscular dystrophy Centronuclear myopathy Core myopathy Myopathy Developmental myosin heavy chain RNA interference Becker muscular dystrophy BMD Gene therapy Adult patients Dynamin 2 Cell proliferation Cellular neuroscience Autophagosome Actin DNM2 Dynamine Biomarkers Adhesion Allele specific RNA interference Dystrophie musculaire de Duchenne Duchenne muscular dystrophy DMD Cross-presentation Autophagosome maturation BAR proteins Lamin Cavins Myopathie BAF Cytoskeleton Dullard Cell signaling Congenital myopathy Muscle Animal models of human disease Autophagy Alpha-actinin-2 Diaphragm Biophysics Adeno-associated virus AFM DMyHC Dynamin Outflow tract Nesprin Atrial heart defects Mechanotransduction Dystrophie musculaire d'Emery Dreifuss Cross-bridge kinetics Clathrine Disease heterogeneity A-type lamins Allele-specific silencing therapy Neural crest cells Adeno-associated virus vector Disease modifiers Nuclear envelope AAV8 Domaine LEM Migration Allele‐specific silencing therapy Cytosquelette Duchenne Muscular Dystrophy ACTN2 Autophagy cellular Cardiotoxin AAV Antisense oligonucleotides Dynamin overexpression Cavéoles CTL Actin nucleus Skeletal muscle Endocytosis Coeur Amphiphysin Cellules de crête neurale Muscular dystrophy Caveolae Charcot-Marie-Tooth Clathrin Nucleus Allele-specific silencing Cardiomyopathies Dominant centronuclear myopathy Atrial cardiac defects BMP signaling Correlative microscopy Myosin Skin CAV-3 gene Cell migration Satellite cell Developmental biology Autosomal dominant centronuclear myopathy Caveolin Caveolins Ctdnep1 Adeno-Associated virus AD-CNM